Electroporation Enhanced Effect of Dystrophin Splice Switching PNA Oligomers in Normal and Dystrophic Muscle
Peptide nucleic acid (PNA) is a synthetic DNA mimic that has shown potential for discovery of novel splice switching antisense drugs. However, in vivo cellular delivery has been a limiting factor for development, and only few successful studies have been reported. As a possible modality for improvem...
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Main Authors: | Camilla Brolin (Author), Takehiko Shiraishi (Author), Pernille Hojman (Author), Thomas O Krag (Author), Peter E Nielsen (Author), Julie Gehl (Author) |
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Format: | Book |
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Elsevier,
2015-01-01T00:00:00Z.
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Online Access: | Connect to this object online. |
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