Oncology drugs for orphan indications: how are HTA processes evolving for this specific drug category?
Elizabeth M Adkins,1 Lindsay Nicholson,1 David Floyd,1 Mark Ratcliffe,1 Helene Chevrou-Severac2 1PHMR, London, UK; 2Takeda Pharmaceuticals AG, Zurich, Switzerland Abstract: Orphan drugs (ODs) are intended for the diagnosis, prevention, or treatment of rare diseases. Many cancer subtypes, including a...
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Dove Medical Press,
2017-06-01T00:00:00Z.
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