Adenylosuccinic Acid Is a Non-Toxic Small Molecule In Vitro and In Vivo

Adenylosuccinic acid (ASA) is a small molecule dicarboxylate that could be a strong clinical development candidate for inherited myopathies involving dysregulated purine nucleotide metabolism. Currently, there are no published pharmacokinetic/dynamic or toxicology data available, although 10-year cl...

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Autores principales: Cara A. Timpani (Autor), Lorna Rasmussen (Autor), Emma Rybalka (Autor)
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Publicado: MDPI AG, 2023-10-01T00:00:00Z.
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Número de Clasificación: A1234.567
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