Matched Unrelated Hematopoietic Stem Cell Transplant in Juvenile-Onset Krabbe's Disease

• Main Authors: Ruchira Misra (Author), Sunil Bhat (Author), Suhani Shah (Author), Anaita Hegde (Author), Hiren Panwala (Author), Divyata Hingwala (Author)
• Formato: Livro
• Publicado em: Wolters Kluwer Medknow Publications, 2022-01-01T00:00:00Z.
• Assuntos: article
• Acesso em linha: Connect to this object online.

Background: Krabbe's disease is a neurodegenerative condition caused by a deficiency of a lysosomal enzyme, galactocerebrosidase (GALC), found mainly in the brain. There are four variants based on the age of onset: Infantile, late infantile, juvenile, and adult. Hematopoietic stem cell transpla...