Systematic Review of Presymptomatic Treatment for Spinal Muscular Atrophy

Spinal muscular atrophy (SMA) causes the degeneration of motor neurons in the spinal cord. Treatments including nusinersen, risdiplam, and onasemnogene abeparvovec have been shown to be effective in reducing symptoms, with recent studies suggesting greater effectiveness when treatment is initiated i...

Full description

Saved in:
Bibliographic Details
Main Authors: Katy Cooper (Author), Gamze Nalbant (Author), Anthea Sutton (Author), Sue Harnan (Author), Praveen Thokala (Author), Jim Chilcott (Author), Alisdair McNeill (Author), Alice Bessey (Author)
Format: Book
Published: MDPI AG, 2024-08-01T00:00:00Z.
Subjects:
Online Access:Connect to this object online.
Tags: Add Tag
No Tags, Be the first to tag this record!

Internet

Connect to this object online.

3rd Floor Main Library

Holdings details from 3rd Floor Main Library
Call Number: A1234.567
Copy 1 Available