Eliciting health state utilities for Aromatic L-amino Acid Decarboxylase (AADC) deficiency: a UK vignette study

Abstract Purpose The aim of this study was to generate health state utilities for aromatic L-amino acid decarboxylase (AADC) deficiency, a rare genetic, lifelong neurogenerative condition predominantly manifesting in young infants. Methods Participants were presented with health state vignettes. The...

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Egile Nagusiak: Adam B. Smith (Egilea), Andria Hanbury (Egilea), Katharina Buesch (Egilea)
Formatua: Liburua
Argitaratua: SpringerOpen, 2021-12-01T00:00:00Z.
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