Current Drug Repurposing Strategies for Rare Neurodegenerative Disorders

• Главные авторы: Sweta Shah (Автор), Marc Marie Dooms (Автор), Sofia Amaral-Garcia (Автор), Mariana Igoillo-Esteve (Автор)
• Формат: ‌
• Опубликовано: Frontiers Media S.A., 2021-12-01T00:00:00Z.
• Предметы: article
• Online-ссылка: Connect to this object online.

Rare diseases are life-threatening or chronically debilitating low-prevalent disorders caused by pathogenic mutations or particular environmental insults. Due to their high complexity and low frequency, important gaps still exist in their prevention, diagnosis, and treatment. Since new drug discover...