Topical Sirolimus 0.2% Gel for the Management of Tuberous Sclerosis Complex-Related Cutaneous Manifestations: An Interim Analysis of Postmarketing Surveillance in Japan

Abstract Introduction Tuberous sclerosis complex (TSC) is a rare autosomal dominant genetic disorder affecting several organs, including skin. We sought to assess the real-world effectiveness and safety of a topical sirolimus 0.2% gel treatment for TSC-related cutaneous manifestations. Methods We co...

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Autori principali: Akemi Egami (Autore), Shinji Takahashi (Autore), Takeshi Kokubo (Autore), Sreedevi Boggarapu (Autore), Eric Beresford (Autore)
Natura: Libro
Pubblicazione: Adis, Springer Healthcare, 2023-03-01T00:00:00Z.
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