Lipid Nanoparticle-Mediated Liver-Specific Gene Therapy for Hemophilia B
<b>Background</b>/<b>Objectives</b>: Hemophilia B is a hereditary bleeding disorder due to the production of liver malfunctional factor IX (FIX). Gene therapy with viral vectors offers a cure. However, applications are limited due to pre-existing antibodies, eligibility for c...
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| Main Authors: | , , , , , |
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| Format: | Book |
| Published: |
MDPI AG,
2024-11-01T00:00:00Z.
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| Online Access: | Connect to this object online. |
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