State of the Art on Approved Cystic Fibrosis Transmembrane Conductance Regulator (<i>CFTR</i>) Modulators and Triple-Combination Therapy

• Hoofdauteurs: Aniello Meoli (Auteur), Valentina Fainardi (Auteur), Michela Deolmi (Auteur), Giulia Chiopris (Auteur), Francesca Marinelli (Auteur), Caterina Caminiti (Auteur), Susanna Esposito (Auteur), Giovanna Pisi (Auteur)
• Formaat: Boek
• Gepubliceerd in: MDPI AG, 2021-09-01T00:00:00Z.
• Onderwerpen: article
• Online toegang: Connect to this object online.

Cystic fibrosis (CF) is the most common life-limiting inherited disease in Caucasian populations, affecting approximately 80,000 people worldwide. CF is a complex multi-organ monogenic autosomal recessive disorder caused by a mutation in cystic fibrosis transmembrane conductance regulator (<i>...