State of the Art on Approved Cystic Fibrosis Transmembrane Conductance Regulator (<i>CFTR</i>) Modulators and Triple-Combination Therapy

• Main Authors: Aniello Meoli (Author), Valentina Fainardi (Author), Michela Deolmi (Author), Giulia Chiopris (Author), Francesca Marinelli (Author), Caterina Caminiti (Author), Susanna Esposito (Author), Giovanna Pisi (Author)
• Format: Book
• Published: MDPI AG, 2021-09-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Cystic fibrosis (CF) is the most common life-limiting inherited disease in Caucasian populations, affecting approximately 80,000 people worldwide. CF is a complex multi-organ monogenic autosomal recessive disorder caused by a mutation in cystic fibrosis transmembrane conductance regulator (<i>...