Newborn Screening and Treatment of Phenylketonuria: Projected Health Outcomes and Cost-Effectiveness

• Главные авторы: Huey-Fen Chen (Автор), Angela M. Rose (Автор), Susan Waisbren (Автор), Ayesha Ahmad (Автор), Lisa A. Prosser (Автор)
• Формат: ‌
• Опубликовано: MDPI AG, 2021-05-01T00:00:00Z.
• Предметы: article
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The objective of this study was to evaluate the cost-effectiveness of newborn screening and treatment for phenylketonuria (PKU) in the context of new data on adherence to recommended diet treatment and a newly available drug treatment (sapropterin dihydrochloride). A computer simulation model was de...