Newborn Screening and Treatment of Phenylketonuria: Projected Health Outcomes and Cost-Effectiveness

• मुख्य लेखकों: Huey-Fen Chen (लेखक), Angela M. Rose (लेखक), Susan Waisbren (लेखक), Ayesha Ahmad (लेखक), Lisa A. Prosser (लेखक)
• स्वरूप: पुस्तक
• प्रकाशित: MDPI AG, 2021-05-01T00:00:00Z.
• विषय: article
• ऑनलाइन पहुंच: Connect to this object online.

The objective of this study was to evaluate the cost-effectiveness of newborn screening and treatment for phenylketonuria (PKU) in the context of new data on adherence to recommended diet treatment and a newly available drug treatment (sapropterin dihydrochloride). A computer simulation model was de...