An open-label clinical trial of agalsidase alfa enzyme replacement therapy in children with Fabry disease who are naïve to enzyme replacement therapy

• Egile Nagusiak: Goker-Alpan O (Egilea), Longo N (Egilea), McDonald M (Egilea), Shankar SP (Egilea), Schiffmann R (Egilea), Chang P (Egilea), Shen Y (Egilea), Pano A (Egilea)
• Formatua: Liburua
• Argitaratua: Dove Medical Press, 2016-05-01T00:00:00Z.
• Gaiak: article
• Sarrera elektronikoa: Connect to this object online.

Ozlem Goker-Alpan,1 Nicola Longo,2 Marie McDonald,3 Suma P Shankar,4,5 Raphael Schiffmann,6 Peter Chang,7 Yinghua Shen,7 Arian Pano7 1Lysosomal Disorders Unit, Fairfax, VA, 2University of Utah, Salt Lake City, UT, 3Department of Pediatrics, Duke University, Durham, NC, 4Department of Ophthalmology,...