An open-label clinical trial of agalsidase alfa enzyme replacement therapy in children with Fabry disease who are naïve to enzyme replacement therapy

• Main Authors: Goker-Alpan O (Author), Longo N (Author), McDonald M (Author), Shankar SP (Author), Schiffmann R (Author), Chang P (Author), Shen Y (Author), Pano A (Author)
• Format: Book
• Published: Dove Medical Press, 2016-05-01T00:00:00Z.
• Subjects: article
• Online Access: Connect to this object online.

Ozlem Goker-Alpan,1 Nicola Longo,2 Marie McDonald,3 Suma P Shankar,4,5 Raphael Schiffmann,6 Peter Chang,7 Yinghua Shen,7 Arian Pano7 1Lysosomal Disorders Unit, Fairfax, VA, 2University of Utah, Salt Lake City, UT, 3Department of Pediatrics, Duke University, Durham, NC, 4Department of Ophthalmology,...