Hakutulokset - Jacques P. Tremblay

Delivery of RNAs to Specific Organs by Lipid Nanoparticles for Gene Therapy Tekijä Kelly Godbout, Jacques P. Tremblay

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Increased Expression of Laminin Subunit Alpha 1 Chain by dCas9-VP160 Tekijä Arnaud Perrin, Joël Rousseau, Jacques P. Tremblay

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CRISPR-Cas9 delivery strategies with engineered extracellular vesicles Tekijä Yaoyao Lu, Kelly Godbout, Gabriel Lamothe, Jacques P. Tremblay

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A Potential New Therapeutic Approach for Friedreich Ataxia: Induction of Frataxin Expression With TALE Proteins Tekijä Pierre Chapdelaine, Zoé Coulombe, Amina Chikh, Catherine Gérard, Jacques P Tremblay

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Base editing strategy for insertion of the A673T mutation in the APP gene to prevent the development of AD in vitro Tekijä Antoine Guyon, Joël Rousseau, Francis-Gabriel Bégin, Tom Bertin, Gabriel Lamothe, Jacques P. Tremblay

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Increased Frataxin Expression Induced in Friedreich Ataxia Cells by Platinum TALE-VP64s or Platinum TALE-SunTag Tekijä Khadija Cherif, Catherine Gérard, Joël Rousseau, Dominique L. Ouellet, Pierre Chapdelaine, Jacques P. Tremblay

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Emerging Perspectives on Prime Editor Delivery to the Brain Tekijä Eli BenDavid, Sina Ramezanian, Yaoyao Lu, Joël Rousseau, Avi Schroeder, Marc Lavertu, Jacques P. Tremblay

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Prime editing optimized RTT permits the correction of the c.8713C>T mutation in DMD gene Tekijä Cedric Happi Mbakam, Joel Rousseau, Yaoyao Lu, Anne Bigot, Kamel Mamchaoui, Vincent Mouly, Jacques P. Tremblay

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Efficient Restoration of the Dystrophin Gene Reading Frame and Protein Structure in DMD Myoblasts Using the CinDel Method Tekijä Jean-Paul, Dominique L Ouellet, Xavier Barbeau, Joël Rousseau, Pierre Chapdelaine, Patrick Lagüe, Jacques P Tremblay

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Targeted Gene Addition of Microdystrophin in Mice Skeletal Muscle via Human Myoblast Transplantation Tekijä Basma F Benabdallah, Arnaud Duval, Joel Rousseau, Pierre Chapdelaine, Michael C Holmes, Eli Haddad, Jacques P Tremblay, Christian M Beauséjour

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